Cell & Gene Therapies

RNAs are very active players in cell biology... they carry instructions for making proteins, turn genes on and off, aid chemical reactions, slice and dice other RNAs, and build proteins. Here's a simple map to understand how can we use them as drugs #quick_notes_LP

Hundreds of trials are underway with some major therapeutic breakthroughs… Will their use become ubiquitous? Or will its adoption be slow? Here’s a map of the things that matter when discussing CMC issues to develop an advanced therapy.

#quick_notes_LP